Gene2 diseases

TNFRSF1A

5 variant(s) documented across Adult-Onset Still's Disease, TNF Receptor-Associated Periodic Syndrome

Found across diseases

Variants

VariantTypeFrequency in diseaseSignificanceAlso found in
Rare variants associated with AOSDgermlineRare; particularly relevant in patients with severe/refractory disease coursesTNFRSF1A is the causative gene for TRAPS (TNF receptor-associated periodic syndrome); its association with AOSD further supports genetic overlap with monogenic autoinflammatory diseasesTRAPS (Causative (autosomal dominant)); Other periodic fevers (Variable)
Cysteine-disrupting mutations (multiple)germline~27% of Eurofever patientsHigh-penetrance pathogenic variants. Disrupt disulfide bonds in CRD1/CRD2 of the TNFR1 extracellular domain. Associated with severe phenotype and high amyloidosis risk (24% vs 2% for non-cysteine).
T50M (p.Thr79Met)germline~10% of Eurofever patientsMost common high-penetrance pathogenic variant. Affects a conserved hydrogen bond critical for protein folding in CRD1. Despite not disrupting a cysteine, carries high disease penetrance and amyloidosis risk similar to cysteine mutations.
R92Q (p.Arg121Gln)germline~34% of Eurofever patients (most common variant overall)Low-penetrance variant of uncertain pathogenic significance. Present in 1.2–4% of healthy Caucasians. Associated with milder disease, shorter episodes, less familial aggregation (19% vs 64%), and higher spontaneous resolution rates. Classified as INSAID Group B (uncertain significance).Multiple sclerosis (Occasional co-occurrence reported)
P46L (p.Pro75Leu)germlineLow-penetrance, uncertain pathogenicityAnother low-penetrance variant. Found at high frequency in sub-Saharan West African populations. Clinical significance debated — may be a benign polymorphism in some ethnic backgrounds.

Clinical implications

Rare variants associated with AOSD

Patients with TNFRSF1A variants may have more challenging disease courses and higher likelihood of requiring biologic therapy

Testing: Sanger sequencing, Next-generation sequencing

Cysteine-disrupting mutations (multiple)

Aggressive treatment with IL-1 blockade recommended. Intensive SAA monitoring for amyloidosis. Higher penetrance (93%).

Testing: Sanger sequencing, next-generation sequencing panel, whole exome sequencing

T50M (p.Thr79Met)

Classified as pathogenic (INSAID Group A). Requires biologic treatment and amyloidosis surveillance.

Testing: Sanger sequencing, targeted gene panel

R92Q (p.Arg121Gln)

Diagnosis of TRAPS should be made cautiously. Colchicine or NSAIDs may suffice. Amyloidosis risk is very low. Some cases may represent coincidental finding.

Testing: Sanger sequencing, targeted gene panel

P46L (p.Pro75Leu)

Context-dependent interpretation required. May be benign in African populations where allele frequency is high.

Testing: Sanger sequencing, targeted gene panel

Related hypotheses

Genetic susceptibility via HLA polymorphisms and autoinflammatory gene variants predisposes to AOSD

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emerging·12 studies

Sources (9)

DetailsSigrist S et al. (2018) Evidence for genetic overlap between adult onset Still's disease and hereditary periodic fever syndromesDOI
DetailsAksentijevich I et al. (2001) The tumor-necrosis-factor receptor-associated periodic syndrome: new mutations in TNFRSF1A, ancestral origins, genotype-phenotype studies, and evidence for further genetic heterogeneity of periodic feversDOI
DetailsHull KM et al. (2002) The TNF receptor-associated periodic syndrome (TRAPS): emerging concepts of an autoinflammatory disorderDOI
DetailsLachmann HJ et al. (2014) The phenotype of TNF receptor-associated autoinflammatory syndrome (TRAPS) at presentation: a series of 158 cases from the Eurofever/EUROTRAPS international registryDOI
DetailsMcDermott MF et al. (1999) Germline mutations in the extracellular domains of the 55 kDa TNF receptor, TNFR1, define a family of dominantly inherited autoinflammatory syndromesDOI
DetailsPapa R et al. (2021) INSAID variant classification and Eurofever criteria guide optimal treatment strategy in patients with TRAPS: data from the Eurofever RegistryDOI
DetailsPelagatti MA et al. (2011) Long-term clinical profile of children with the low-penetrance R92Q mutation of the TNFRSF1A geneDOI
DetailsRuiz-Ortiz E et al. (2017) Disease phenotype and outcome depending on age at disease onset in patients carrying the R92Q low-penetrance variant in TNFRSF1A geneDOI
DetailsCudrici C et al. (2020) Revisiting TNF Receptor-Associated Periodic Syndrome (TRAPS): Current PerspectivesDOI