Diseases

Each disease page is a deep, evidence-linked reference built from published research. More diseases are added based on community requests.

Adult-Onset Still's Disease

Adult-onset Still's disease (AOSD) is a rare systemic autoinflammatory disorder characterized by the classic triad of quotidian (daily) spiking fevers, salmon-colored evanescent rash, and arthritis or arthralgia.

Autoinflammatory

Chronic Rhinosinusitis with Nasal Polyps

Chronic rhinosinusitis with nasal polyps (CRSwNP) is a chronic inflammatory disease of the sinonasal mucosa characterised by bilateral polyp growth, persistent nasal obstruction, anosmia, and impaired quality of life.

InflammatoryOtorhinolaryngologic

Cryopyrin-Associated Periodic Syndromes

Cryopyrin-associated periodic syndromes (CAPS) are a spectrum of rare, inherited autoinflammatory disorders caused by gain-of-function mutations in the NLRP3 gene encoding cryopyrin.

AutoinflammatoryMonogenic

Familial Mediterranean Fever

Familial Mediterranean Fever (FMF) is the most common monogenic autoinflammatory disease worldwide, caused by gain-of-function mutations in the MEFV gene encoding pyrin.

AutoinflammatoryMonogenic

Hypocomplementemic Urticarial Vasculitis Syndrome

Hypocomplementemic urticarial vasculitis syndrome (HUVS) is a rare immune complex-mediated small vessel vasculitis characterised by chronic urticaria lasting >6 months, persistent hypocomplementemia (low C1q, C3, C4), and leukocytoclastic vasculitis on skin biopsy.

400 casesAutoimmuneVasculitis

POEMS Syndrome

POEMS syndrome is a rare paraneoplastic disorder caused by an underlying clonal plasma cell neoplasm.

HematologicParaneoplastic

Schnitzler Syndrome

Rare acquired autoinflammatory disorder characterised by chronic urticarial rash with monoclonal IgM gammopathy and systemic inflammation.

748 casesAutoinflammatoryHematologic

Systemic Mastocytosis

Systemic mastocytosis is a clonal hematologic neoplasm characterized by abnormal proliferation and accumulation of neoplastic mast cells in one or more extracutaneous organs, primarily the bone marrow.

HematologicMast cell neoplasm

TNF Receptor-Associated Periodic Syndrome

TNF Receptor-Associated Periodic Syndrome (TRAPS) is the most common autosomal dominant autoinflammatory disease, caused by heterozygous mutations in the TNFRSF1A gene encoding the type 1 TNF receptor (TNFR1).

1,000 casesAutoinflammatoryMonogenic

Waldenström's Macroglobulinemia

Waldenström's macroglobulinemia is an indolent B-cell lymphoproliferative disorder characterised by bone marrow infiltration with clonal lymphoplasmacytic cells that secrete monoclonal IgM.

HematologicLymphoproliferative