Efficacy and Safety of Midostaurin in Advanced Systemic Mastocytosis

Key Findings

• ●Overall response rate 60% in AdvSM
• ●45% major response (complete resolution of organ damage)
• ●Median OS 28.7 months; median PFS 14.1 months
• ●Median 59% reduction in MC burden and 58% reduction in serum tryptase

Referenced in (1 disease)