incrementalNew research

BTK degraders (PROTACs) enter clinical trials for B-cell malignancies

Waldenström's Macroglobulinemia

Summary

BTK degraders such as BGB-16673 and NX-5948 entered clinical trials for B-cell malignancies including WM. Unlike BTK inhibitors which require sustained binding, degraders eliminate the BTK protein entirely via the proteasome. This mechanism may overcome acquired resistance mutations at the BTK C481 binding site that limit covalent BTK inhibitor efficacy.

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ID: waldenstroms-macroglobulinemia-update-3Type: new_researchImpact: incremental