Gene

ASXL1

1 variant(s) documented across Systemic Mastocytosis

Variants

VariantTypeFrequency in diseaseSignificanceAlso found in
Various truncating mutationssomatic~29% of advanced SMEpigenetic regulator (polycomb group protein). Independently predicts inferior survival (HR 3.4). Part of the S/A/R gene panel.MDS/MPN/AML (~10-25%)

Clinical implications

Various truncating mutations

High-risk mutation. Independently predictive of inferior survival alongside CBL.

Testing: next-generation sequencing

Related hypotheses

Hereditary alpha-tryptasemia (HαT) modifies SM phenotype, increasing mediator symptoms and anaphylaxis risk independent of mast cell burden

40
emerging·6 studies