DrugAlternative line

Ibrutinib

BTK inhibitor

Response rate
Complete in case reports
Onset
2 weeks – 3 months
Route
Oral 420mg daily
Line
Alternative
IgM effect
Reduces IgM
Evidence level
default

Evidence summary

The only drug shown to reduce both inflammatory symptoms AND IgM levels. Currently limited to case reports.

Molecular targets

MoleculeRoleExpressionEvidence
MYD88TLR signalling adaptorL265P in ~30%moderate
BTKB-cell receptor kinaseActivemoderate
IgM (monoclonal)Diagnostic paraproteinPresent (obligate)established

Sources (1)

I5Huang Y et al. (2022) Ibrutinib for MYD88 L265P-positive SchnitzlerDOI
Ibrutinib — Drug Profile | Kipine