Zanubrutinib

Second-generation selective BTK inhibitor

Response rate
~95% ORR; 36% VGPR+CR
Onset
Weeks
Route
Oral 160mg BID or 320mg daily
Line
1st
IgM effect
Significant reduction

Evidence summary

Next-generation BTK inhibitor with greater selectivity for BTK. The ASPEN phase III trial demonstrated comparable efficacy to ibrutinib with significantly improved safety: less atrial fibrillation (7.9% vs 23.5%), less hypertension, less diarrhea. Currently recommended as preferred first-line BTK inhibitor by Mayo Clinic guidelines.

Molecular targets (1)

MoleculeRoleExpressionEvidence
BTK (Bruton's Tyrosine Kinase)Key signaling kinase downstream of MYD88Constitutively activatedestablished